A new article about Clinical Effectiveness of Newborn Screening for Spinal Muscular Atrophy is published
A new article about Clinical Effectiveness of Newborn Screening for Spinal Muscular Atrophy - a nonrandomized controlled trial is published.
Researchers demostrated in this nonrandomized controlled trial the effectiveness of newborn screening for infants with SMA in a real-world-setting.
For further information please look here:
https://pubmed.ncbi.nlm.nih.gov/38587854/
To read the full text, please click here: https://jamanetwork.com/journals/jamapediatrics/article-abstract/2817302