The drug Spinraza, used to treat the neurodegenerative disease SMA, has been approved for the treatment of adults in October 2023. So far, it has only been approved for use by children. For more information please click here.

Today we celebrate International Neonatal Screening Day! 😊

Check out the latest publication on #newbornscreening issued by RARE Revolution Magazine. Our Steering Committee member Kacper Rucinski, co-founder of SMA Foundation Poland, speaks about the challenges of ensuring Europe-wide newborn screening for SMA.

The analysis assessing the cost-effectiveness of newborn screening for SMA in England by Novartis has been published online in Neurology and Therapy . The publication might be useful especially for countries where newborn screening is not yet implemented. For further information please look here.